RARE Ultragenyx Pharmaceutical Inc.

P/E --
Forward P/E --
Price/Sales 1.995
Beta 0.315
Div Yield --
Market Cap --

Company Analysis

Latest News

Ultragenyx Announces FDA Full Approval for FAYUVI™, First-Ever Gene Therapy for MPS IIIA

Ultragenyx Announces FDA Full Approval for FAYUVI™, First-Ever Gene Therapy for MPS IIIA

Ultragenyx Pharmaceutical Inc. announced it received standard full approval from the U.S. Food and Drug Administration (FDA) for FAYUVI™ (rebisufligene...

🟢 Ultragenyx is trading 11.57% up today as XBI rises amid renewed M&A optimism

Ultragenyx is trading at $14.37, up 11.57%, as biotechnology rebounds and XBI rises 2.55%. • The rebound reflects a stronger industry outlook and renewed M&A...

🟢 Ultragenyx is trading 5.5% up today amid a broad biotechnology rebound

Ultragenyx is trading 5.5% up at $13.59, alongside a broad biotechnology rebound and stronger overall risk appetite. - No new company-specific announcement...

🟢 Ultragenyx is trading 5% up today as rebound appears to reflect post-selloff trading

Ultragenyx is trading 5% up at $15.62, rebounding after its September 3, 2026 close of $14.85, when shares fell 44.03%. - The earlier collapse followed...

🔴 Ultragenyx is trading 47% down today after apazunersen fails Phase 3 Aspire trial

Ultragenyx is trading 47% down at $14.03 after apazunersen (GTX-102) failed its Phase 3 Aspire trial in Angelman syndrome. - The treatment missed both its...

Ultragenyx's Angelman Drug Fails Its Biggest Test — Now What Is Left to Support a $1.4 Billion Company?

Ultragenyx's Angelman Drug Fails Its Biggest Test — Now What Is Left to Support a $1.4 Billion Company?

Shares of Ultragenyx Pharmaceutical cratered 45% overnight after its most-watched experimental therapy — a gene-silencing drug for Angelman syndrome, a rare...

🔴 Ultragenyx is trading 45.53% down in pre-market after Phase 3 Aspire study failed primary endpoints

Ultragenyx is trading at $14.45 (-45.53%) in pre-market after its Phase 3 Aspire study of apazunersen failed to meet primary and key secondary endpoints. -...

Ultragenyx's Phase 3 Angelman Syndrome Trial for Apazunersen Fails to Meet Endpoints

Ultragenyx's Phase 3 Angelman Syndrome Trial for Apazunersen Fails to Meet Endpoints

Ultragenyx Pharmaceutical Inc. announced that its Phase 3 Aspire study for apazunersen (GTX-102) in patients with Angelman syndrome did not meet its primary or...

🔴 Ultragenyx is trading 43% down in after-hours trading

Ultragenyx is trading 42.82% down at $15.17 after-hours on September 2, 2026, versus the regular-session close; the catalyst remains unclear. - No credible...

🟢 Ultragenyx is trading 4.1% up today after GENGLYCOS FDA approval

Ultragenyx is trading at $26.79 (+4.14%) after the August 19 FDA approval of GENGLYCOS, its first approved gene therapy. - Reuters reported the announcement...

🟢 Ultragenyx is trading 4.64% up today after FDA’s accelerated approval of GENGLYCOS

Ultragenyx is trading 4.64% up now at $26.50 as investors continue responding to the FDA’s accelerated approval of GENGLYCOS, announced August 19, 2026. - The...

🔴 Ultragenyx is trading 4.23% down today amid broader biotech pullback

Ultragenyx is trading 4.23% down at $25.13 amid a broader biotech pullback and weak risk sentiment across U.S. equities. - Ultragenyx announced accelerated...

Ultragenyx Stock Falls, Awaiting FDA Decision on Rare Disease Gene Therapy

Ultragenyx Stock Falls, Awaiting FDA Decision on Rare Disease Gene Therapy

Ultragenyx Pharmaceutical (RARE) shares fell for a second consecutive day on Tuesday, August 18th. Investors are awaiting an FDA decision on DTX401, a gene...

Ultragenyx Lands Its First Gene Therapy — But Can a Tiny Patient Pool Justify the Stock's Leap of Faith?

Ultragenyx Lands Its First Gene Therapy — But Can a Tiny Patient Pool Justify the Stock's Leap of Faith?

Shares of Ultragenyx surged 14% to $29.91 after the FDA granted accelerated approval for the company's first-ever gene therapy, a one-time treatment for a rare...

🟢 Ultragenyx is trading 13.99% up in pre-market after FDA granted accelerated approval for GENGLYCOS

Ultragenyx is trading 13.99% up at $29.91 after FDA granted accelerated approval for GENGLYCOS on August 19, 2026. - GENGLYCOS treats glycogen storage disease...

Ultragenyx Receives FDA Accelerated Approval for GSDIa Gene Therapy GENGLYCOS™

Ultragenyx Receives FDA Accelerated Approval for GSDIa Gene Therapy GENGLYCOS™

Ultragenyx Pharmaceutical announced that the U.S. Food and Drug Administration (FDA) has granted accelerated approval for its gene therapy, GENGLYCOS™...

🟢 Ultragenyx is trading 10% up in after-hours trading with no verified company-specific catalyst

Ultragenyx is trading 10% up at $28.86 after closing at $26.24 on August 19, 2026, with no verified company-specific announcement released after the regular...

🔴 Ultragenyx is trading 4.1% down today as higher yields pressure biotech stocks

Ultragenyx is trading 4.1% down now at $25.07, primarily as higher yields and broader risk-off trading pressure growth-oriented biotechnology stocks. - No...

Ultragenyx Settles DOJOLVI® Patent Litigation, Allows Generic Entry in 2033

Ultragenyx Settles DOJOLVI® Patent Litigation, Allows Generic Entry in 2033

Ultragenyx Pharmaceutical Inc. has entered into a settlement agreement with Esjay Pharma to resolve patent litigation related to its drug, DOJOLVI®...

🟢 Ultragenyx is trading 4% up today after record Q2 results beat estimates

Ultragenyx is trading 4.01% up now at $26.95 after investors continued reacting to its record second-quarter results. - Q2 revenue reached $214 million,...